More than two years after the Government committed to adding SMA to newborn testing, families are still waiting ...

A Prescription Drug User Fee Act target date of September 22, 2025 has been set for the application. The Food and Drug Administration (FDA) has accepted for Priority Review the Biologics License ...

What is SMA? The rare genetic condition that Jesy Nelson’s twins have - Former Little Mix star revealed her twin daughters had been diagnosed with Spinal Muscular Atrophy (SMA) Type 1 ...

Former Little Mix singer Jesy Nelson is dealing with yet another heartbreaking truth. The singer and her longtime fiancé Zion Foster have called it quits. The unfortunate news comes just weeks after ...

"Monumental" is how Ashley E. Webb, MD Assistant Professor, Department of Pediatrics, Division of Child & Adolescent Neurology Neuromuscular Program Director, UTHealth, University of Texas Health ...

Spinal Muscular Atrophy, known as SMA Type 1, explained: A Paediatric neurologist shares insight into the condition after former Little Mix singer Jesy Nelson revealed her twins have been diagnosed ...

A couple whose son died from a rare genetic condition are encouraging others to take part in screening which they say could ...

People with spinal muscle atrophy (SMA), an inherited neuromuscular disease, usually experience muscle weakness that impacts movement. New research suggests that electrical spinal cord stimulation ...

"Our preliminary findings show that German children with SMA, despite significant physical disability, have surprisingly good subjective HRQoL." – Erik Landfeldt, MSc, PhD Previous studies have found ...